Regenxbio Inc is a biotechnology company focused on advancing the field of gene therapy for the treatment of rare and debilitating diseases. The company specializes in developing innovative therapies that utilize its proprietary AAV (adeno-associated virus) gene delivery technology, which aims to correct genetic defects and restore normal function at the cellular level. Regenxbio is committed to addressing unmet medical needs through its robust pipeline of product candidates, targeting various conditions, including inherited retinal diseases and neurodegenerative disorders. By harnessing the power of gene therapy, Regenxbio seeks to transform treatment options and improve the quality of life for patients.